Trial Outcomes & Findings for Study of Leptin for the Treatment of Hypothalamic Amenorrhea (NCT NCT00130117)

NCT ID: NCT00130117

Last Updated: 2017-05-17

Results Overview

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

20 participants

Primary outcome timeframe

36 weeks

Results posted on

2017-05-17

Participant Flow

Participant milestones

Participant milestones
Measure
r-metHuLeptin
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Overall Study
STARTED
11
9
Overall Study
COMPLETED
7
6
Overall Study
NOT COMPLETED
4
3

Reasons for withdrawal

Withdrawal data not reported

Baseline Characteristics

Study of Leptin for the Treatment of Hypothalamic Amenorrhea

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
r-metHuLeptin
n=11 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=9 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Total
n=20 Participants
Total of all reporting groups
Age, Categorical
<=18 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Categorical
Between 18 and 65 years
11 Participants
n=99 Participants
9 Participants
n=107 Participants
20 Participants
n=206 Participants
Age, Categorical
>=65 years
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Age, Continuous
26.6 years
STANDARD_DEVIATION 1.4 • n=99 Participants
25.4 years
STANDARD_DEVIATION 1.2 • n=107 Participants
26 years
STANDARD_DEVIATION 1.3 • n=206 Participants
Sex: Female, Male
Female
11 Participants
n=99 Participants
9 Participants
n=107 Participants
20 Participants
n=206 Participants
Sex: Female, Male
Male
0 Participants
n=99 Participants
0 Participants
n=107 Participants
0 Participants
n=206 Participants
Region of Enrollment
United States
11 participants
n=99 Participants
9 participants
n=107 Participants
20 participants
n=206 Participants

PRIMARY outcome

Timeframe: 36 weeks

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=7 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=6 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
the Difference Between the Placebo and Leptin Treated Groups in the Change in Bone Mineral Content(BMC) at the Anteroposterior (AP) Spine From Baseline to 36 Weeks
51.0 g
Interval 43.4 to 58.2
58.2 g
Interval 55.2 to 61.4

SECONDARY outcome

Timeframe: 36 weeks

Population: Only for subjects participating in both phase A and phase B (n=4), bone markers were assessed to see the change over 24 month period. All these patient got metreleptin treatment

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=4 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Bone Markers - Ctx and Sclerostin
CTX
0.60 ng/mL
Interval 0.39 to 0.83
Bone Markers - Ctx and Sclerostin
Sclerostin
0.08 ng/mL
Interval 0.07 to 0.09

SECONDARY outcome

Timeframe: 36 weeks

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=7 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=6 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Body Composition BMI
20.8 BMI-kg/m^2
Standard Error 0.6
21.1 BMI-kg/m^2
Standard Error 0.6

SECONDARY outcome

Timeframe: 36 weeks

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=7 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=6 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Total Body BMD
1.07 g/cm^2
Interval 1.05 to 1.16
1.13 g/cm^2
Interval 1.09 to 1.23

SECONDARY outcome

Timeframe: 36 weeks

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=7 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=6 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Body Fat
23.9 fat %
Standard Error 1.4
20.8 fat %
Standard Error 1.3

SECONDARY outcome

Timeframe: 9 months

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=10 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=9 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Total Body BMD
1.09 g/cm2
Interval 1.06 to 1.15
1.13 g/cm2
Interval 1.1 to 1.23

SECONDARY outcome

Timeframe: 9 months

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=10 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=9 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Lumbar BMD
0.92 g/cm2
Interval 0.8 to 1.03
0.97 g/cm2
Interval 0.9 to 1.01

SECONDARY outcome

Timeframe: 9 months

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=10 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=9 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Radial BMD
0.54 g/cm2
Interval 0.52 to 0.6
0.54 g/cm2
Interval 0.53 to 0.56

SECONDARY outcome

Timeframe: 9months

Outcome measures

Outcome measures
Measure
r-metHuLeptin
n=10 Participants
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=9 Participants
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Hip BMD
0.89 g/cm2
Interval 0.8 to 1.03
0.88 g/cm2
Interval 0.8 to 1.02

Adverse Events

r-metHuLeptin

Serious events: 0 serious events
Other events: 2 other events
Deaths: 0 deaths

Placebo

Serious events: 0 serious events
Other events: 0 other events
Deaths: 0 deaths

Serious adverse events

Adverse event data not reported

Other adverse events

Other adverse events
Measure
r-metHuLeptin
n=11 participants at risk
r-metHuLeptin administered subcutaneously. r-metHuLeptin: Starting dose: 0.08mg/kg once daily Subcutaneous injection. Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily.
Placebo
n=6 participants at risk
placebo Oral Contraceptive Pills (OCPs): Sprintec taken orally once daily. Placebo: placebo (no active medication)
Skin and subcutaneous tissue disorders
local injection site reactions with erythematous rashes
18.2%
2/11 • Number of events 2
11 participants started on the metreleptin arm , although only 7 finished the study. hence participants at risk are 11
0.00%
0/6
11 participants started on the metreleptin arm , although only 7 finished the study. hence participants at risk are 11

Additional Information

Christos Mantzoros

BIDMC

Phone: 6176678630

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place