Trial Outcomes & Findings for Depsipeptide in Unresectable Recurrent or Metastatic Squamous Cell Carcinoma of the Head and Neck (NCT NCT00084682)

NCT ID: NCT00084682

Last Updated: 2021-03-05

Results Overview

Tumor response was assessed every eight weeks per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions as assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; Overall Response (OR) = CR + PR. Stable disease (SD) was defined as having no evidence of response (CR or PR) as best response to therapy, and no evidence of disease progression (appearance of new lesions or \>/= 30% increase in target lesions) at 8 weeks.

Recruitment status

COMPLETED

Study phase

PHASE2

Target enrollment

14 participants

Primary outcome timeframe

Up to 2 years

Results posted on

2021-03-05

Participant Flow

A total of 14 patients were enrolled from one institution between June 2005 and October 2008

Participant milestones

Participant milestones
Measure
Treatment (Romidepsin)
Patients receive FR901228 (depsipeptide) IV at 13 mg/m2 over 4 hours on days 1, 8, and 15. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. romidepsin: Given IV
Overall Study
STARTED
14
Overall Study
COMPLETED
13
Overall Study
NOT COMPLETED
1

Reasons for withdrawal

Reasons for withdrawal
Measure
Treatment (Romidepsin)
Patients receive FR901228 (depsipeptide) IV at 13 mg/m2 over 4 hours on days 1, 8, and 15. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. romidepsin: Given IV
Overall Study
Withdrawal by Subject
1

Baseline Characteristics

Depsipeptide in Unresectable Recurrent or Metastatic Squamous Cell Carcinoma of the Head and Neck

Baseline characteristics by cohort

Baseline characteristics by cohort
Measure
Treatment (Romidepsin)
n=14 Participants
Patients receive FR901228 (depsipeptide) IV at 13 mg/m2 over 4 hours on days 1, 8, and 15. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. romidepsin: Given IV
Age, Continuous
59.0 years
n=85 Participants
Sex: Female, Male
Female
3 Participants
n=85 Participants
Sex: Female, Male
Male
11 Participants
n=85 Participants
Race/Ethnicity, Customized
White
7 participants
n=85 Participants
Race/Ethnicity, Customized
Black
1 participants
n=85 Participants
Race/Ethnicity, Customized
Hispanic
6 participants
n=85 Participants

PRIMARY outcome

Timeframe: Up to 2 years

Tumor response was assessed every eight weeks per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions as assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>=30% decrease in the sum of the longest diameter of target lesions; Overall Response (OR) = CR + PR. Stable disease (SD) was defined as having no evidence of response (CR or PR) as best response to therapy, and no evidence of disease progression (appearance of new lesions or \>/= 30% increase in target lesions) at 8 weeks.

Outcome measures

Outcome measures
Measure
Treatment (Romidepsin)
n=13 Participants
Patients receive FR901228 (depsipeptide) IV at 13 mg/m\^2 over 4 hours on days 1, 8, and 15. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. romidepsin: Given IV
Disease Control (i.e., Achievement of Complete Response, Partial Response, or Stable Disease)
Symptomatic deterioration
2 participants
Interval 1.9 to 45.5
Disease Control (i.e., Achievement of Complete Response, Partial Response, or Stable Disease)
Stable Disease
2 participants
Interval 1.9 to 45.5
Disease Control (i.e., Achievement of Complete Response, Partial Response, or Stable Disease)
Disease progression
9 participants
Interval 1.9 to 45.5

SECONDARY outcome

Timeframe: Up to 2 years

Population: Data not collected. As the first stage goal of 8 patients with disease control was not achievable, further analysis was not done.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: Data not collected. As the first stage goal of 8 patients with disease control was not achievable, further follow up was not done.

All time to event endpoints will be evaluated using Kaplan Meier estimates and survival curves will be generated based on these estimates.

Outcome measures

Outcome data not reported

SECONDARY outcome

Timeframe: Up to 2 years

Population: data not collected

All time to event endpoints will be evaluated using Kaplan Meier estimates and survival curves will be generated based on these estimates. One and two-year survival and median survival time (if attained) will be estimated and reported with 95% confidence limits. If the sample sizes are sufficient, subgroup analysis based on baseline factors will be performed using the log rank test to compare survival curves.

Outcome measures

Outcome data not reported

Adverse Events

Treatment (Romidepsin)

Serious events: 12 serious events
Other events: 11 other events
Deaths: 0 deaths

Serious adverse events

Serious adverse events
Measure
Treatment (Romidepsin)
n=14 participants at risk
Patients receive FR901228 (depsipeptide) IV at 13 mg/m2 over 4 hours on days 1, 8, and 15. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. romidepsin: Given IV
Blood and lymphatic system disorders
Anemia
14.3%
2/14 • Number of events 14
Investigations
Thrombocytopenia
14.3%
2/14 • Number of events 2
Vascular disorders
Hypotension
7.1%
1/14 • Number of events 1
General disorders
Fatigue
35.7%
5/14 • Number of events 5
Metabolism and nutrition disorders
Anorexia
14.3%
2/14 • Number of events 2
Gastrointestinal disorders
Nausea
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
Vomiting
14.3%
2/14 • Number of events 2
Infections and infestations
Lung infection
21.4%
3/14 • Number of events 3
Infections and infestations
Soft tissue infection
7.1%
1/14 • Number of events 1
Vascular disorders
Thrombosis
7.1%
1/14 • Number of events 1

Other adverse events

Other adverse events
Measure
Treatment (Romidepsin)
n=14 participants at risk
Patients receive FR901228 (depsipeptide) IV at 13 mg/m2 over 4 hours on days 1, 8, and 15. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity. romidepsin: Given IV
Vascular disorders
Hypertension
7.1%
1/14 • Number of events 1
Gastrointestinal disorders
Constipation
42.9%
6/14 • Number of events 6
Gastrointestinal disorders
Diarrhea
14.3%
2/14 • Number of events 2
Gastrointestinal disorders
Dyspepsia
7.1%
1/14 • Number of events 1
General disorders
Pain
7.1%
1/14 • Number of events 1

Additional Information

Lisa Escobar-Peralta

Montefiore Medical Center

Phone: 718-379-6866

Results disclosure agreements

  • Principal investigator is a sponsor employee
  • Publication restrictions are in place

Restriction type: LTE60