Lipid nanoparticle gene editing restored up to 100% of normal CFTR function in lab tests
Apr 18, 2026
A lipid nanoparticle gene-editing approach inserted a full healthy CFTR gene into human airway cells and restored 88% to 100% of normal CFTR function in lab tests. The nonviral strategy is intended as a mutation-agnostic path for cystic fibrosis.